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10+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 10 of 10 recruiting trials for “ataxia-pancytopenia-syndrome

NARecruitingNCT06744283

Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia

👨‍⚕️ Sharon A Savage, M.D., National Cancer Institute (NCI)📍 1 site📅 Started Jan 2026View details ↗
Phase 1, PHASE2RecruitingNCT06648096

Afatinib in Patients with Fanconi Anemia (FA) and Advanced Head and Neck Squamous Cell Carcinoma (HNSCC)

👨‍⚕️ Jordi Surrallés, M.D.; Ph.D., Sant Pau's Hospital Research Institute📍 2 sites📅 Started Nov 2024View details ↗
Phase 2RecruitingNCT06014775

Anti-CD38 Antibody Treating Evans Syndrome

👨‍⚕️ Lei Zhang, M.D, Institute of Hematology & Blood Diseases Hospital, China📍 1 site📅 Started Dec 2023View details ↗
NARecruitingNCT05687149

Defining the Natural History of Squamous Cell Carcinoma in Fanconi Anemia

👨‍⚕️ Lisa J McReynolds, M.D., National Cancer Institute (NCI)📍 1 site📅 Started Mar 2023View details ↗
NARecruitingNCT05973656

Role of Acetaldehyde in the Development of Oral Cancer

👨‍⚕️ Balbo Silvia, PhD📍 1 site📅 Started Jul 2022View details ↗
Phase 1, PHASE2RecruitingNCT04784052

Depleted Donor Stem Cell Transplant in Children and Adults With Fanconi Anemia After Being Conditioned With a Regimen Containing Briquilimab

👨‍⚕️ Rajni Agarwal, MD, Stanford University📍 1 site📅 Started Dec 2021View details ↗
NAEnrolling by InvitationNCT04437771

Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

🏥 Rocket Pharmaceuticals Inc.📍 1 site📅 Started Jun 2020View details ↗
Phase 2RecruitingNCT03579875

Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders

👨‍⚕️ Margaret MacMillan, MD, Msc, FRCPC, Masonic Cancer Center, University of Minnesota📍 1 site📅 Started Nov 2018View details ↗
Phase 2RecruitingNCT02143830

HSCT for Patients With Fanconi Anemia Using Risk-Adjusted Chemotherapy

👨‍⚕️ Parinda Mehta, MD, CCHMC📍 3 sites📅 Started Apr 2014View details ↗
RecruitingNCT02877706

French Registry of Adult Patients With Immune Thrombocytopenia and Autoimmune Hemolytic Anemia

👨‍⚕️ Moulis Guillaume, MD PhD, University Hopsital Toulouse📍 1 site📅 Started Jun 2013View details ↗

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