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10+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 10 of 10 recruiting trials for “alazami-syndrome

RecruitingNCT07293897

A Database Study of Maralixibat (TAK-625) in Participants With Alagille Syndrome (ALGS) and Progressive Familial Intrahepatic Cholestasis (PFIC)

👨‍⚕️ Study Director, Takeda📍 1 site📅 Started Jan 2026View details ↗
Phase 4RecruitingNCT07290257

Long-Term Low-Intervention SafEty and Clinical Outcomes Clinical Study of LivmArli® in Patients With Alagille Syndrome in the European Union (LEAP-EU)

🏥 Mirum Pharmaceuticals, Inc.📍 13 sites📅 Started Sep 2025View details ↗
RecruitingNCT06850038

A Study Observing the Long-term, Effectiveness and Safety of Odevixibat (Bylvay) in Patients With Alagille Syndrome (ALGS) Who Are Receiving Ongoing Treatment

👨‍⚕️ Ipsen Medical, Director, Ipsen📍 8 sites📅 Started Apr 2025View details ↗
Phase 4RecruitingNCT06499948

Albuminuria Lowering Effect of Dapagliflozin, Spironolactone and Their Combination in Adult Patients with Alport Syndrome (COMBINE-ALPORT)

🏥 Stefan Lujinschi📍 1 site📅 Started Feb 2024View details ↗
RecruitingNCT06193928

Long-Term SafEty and Clinical Outcomes of LivmArli in Patients in the United States (LEAP-US)

🏥 Mirum Pharmaceuticals, Inc.📍 8 sites📅 Started Sep 2023View details ↗
RecruitingNCT06526741

ASF Alport Patient Registry

👨‍⚕️ Benjamin A Weinstock, PhD, Alport Syndrome Foundation📍 1 site📅 Started Aug 2023View details ↗
Phase 3RecruitingNCT05035030

Long-term Safety and Efficacy of Odevixibat in Patients With Alagille Syndrome

👨‍⚕️ Ipsen Medical Director, Ipsen📍 20 sites📅 Started Sep 2021View details ↗
RecruitingNCT04947813

Genotype-Phenotype Correlations in Patients With Alport Syndrome

🏥 Xinhua Hospital, Shanghai Jiao Tong University School of Medicine📍 1 site📅 Started Jan 2021View details ↗
RecruitingNCT05927467

Eurbio-Alport (RaDiCo Cohort) (RaDiCo Eurbio-Alport)

👨‍⚕️ Laurence Heidet, PHD, INSERM U933📍 1 site📅 Started May 2017View details ↗
RecruitingNCT02378805

Alport Therapy Registry - European Initiative Towards Delaying Renal Failure in Alport Syndrome

👨‍⚕️ Oliver Gross, MD, University Hospital Goettingen📍 1 site📅 Started Jul 1995View details ↗

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