🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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Showing 1 of 1 recruiting trials for “alacrimia-choreoathetosis-liver-dysfunction-syndrome”

Phase 1, PHASE2RecruitingNCT06199531 ↗

Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency

🏥 Grace Science, LLC📍 3 sites📅 Started Feb 2024View details ↗

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