🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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5+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 5 of 5 recruiting trials for “Steinert myotonic dystrophy”

Phase 2Enrolling by InvitationNCT06926621 ↗

A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic Dystrophy Type I

🏥 Vertex Pharmaceuticals Incorporated📍 11 sites📅 Started Apr 2025View details ↗
Phase 1, PHASE2RecruitingNCT06185764 ↗

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

🏥 Vertex Pharmaceuticals Incorporated📍 26 sites📅 Started Feb 2024View details ↗
Phase 1, PHASE2RecruitingNCT05481879 ↗

Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1

🏥 Dyne Therapeutics📍 17 sites📅 Started Sep 2022View details ↗
RecruitingNCT06075693 ↗

Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy

👨‍⚕️ Thurman M Wheeler, MD, Massachusetts General Hospital📍 1 site📅 Started Aug 2022View details ↗
Enrolling by InvitationNCT06979024 ↗

A Registered Observational Cohort Study of Myotonic Dystrophy Type 1

🏥 First Affiliated Hospital of Fujian Medical University📍 1 site📅 Started Jan 2008View details ↗

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