🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

1+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Clinical trial records are synced from ClinicalTrials.gov.

Showing 1 of 1 recruiting trials for “Spinal Muscular Atrophy”

Phase 1, PHASE2Enrolling by InvitationNCT05152823 ↗

Gene Therapy for IGHMBP2-Related Diseases

👨‍⚕️ Megan Waldrop, MD, Nationwide Children's Hospital📍 1 site📅 Started Nov 2021View details ↗

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