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10+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 10 of 10 recruiting trials for “Sickle cell anemia

Phase 1RecruitingNCT06647979

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

🏥 Daniel Bauer📍 1 site📅 Started Dec 2025View details ↗
Phase 1RecruitingNCT05904093

Study to Evaluate the Safety and Tolerability of Escalating Doses of Fostamatinib in Subjects With Stable Sickle Cell Disease

👨‍⚕️ Swee Lay Thein, M.D., National Heart, Lung, and Blood Institute (NHLBI)📍 1 site📅 Started Dec 2024View details ↗
NARecruitingNCT06529874

Pressure Pain Tolerance in Relation to Balance and Strength in Children

👨‍⚕️ Shimaa A Ahmed, PHD, Head of Haematology Dept, Faculty of Medicine, Alexandria University📍 1 site📅 Started Feb 2024View details ↗
Phase 3RecruitingNCT05285917

Promoting Utilization and Safety of Hydroxyurea Using Precision in Africa

👨‍⚕️ Patrick T McGann, MD, MS, Rhode Island Hospital and Hasbro Children's Hospital📍 1 site📅 Started Nov 2023View details ↗
RecruitingNCT06250595

European Rare Blood Disorders Platform (ENROL)

👨‍⚕️ María del Mar Manú Pereira, PhD, Vall d'Hebron Institut de Recerca / University Hospital Vall d'Hebron (VHIR / HUVH)📍 1 site📅 Started Jul 2022View details ↗
Phase 2RecruitingNCT04201210

A Trial to Assess Haploidentical T-depleted Stem Cell Transplantation in Patients With SCD

👨‍⚕️ Selim Corbacioglu, MD, University Hospital of Regensburg📍 9 sites📅 Started Jun 2021View details ↗
Phase 3Enrolling by InvitationNCT04208529

A Long-term Follow-up Study in Participants Who Received CTX001

🏥 Vertex Pharmaceuticals Incorporated📍 20 sites📅 Started Jan 2021View details ↗
Phase 2Enrolling by InvitationNCT03948867

Stroke Prevention With Hydroxyurea Enabled Through Research and Education (SPHERE)

🏥 Children's Hospital Medical Center, Cincinnati📍 2 sites📅 Started Apr 2019View details ↗
RecruitingNCT03685721

Genotype -Phenotype Correlation of PKLR Variants With Pyruvate Kinase, 2,3-Diphosphglycerate and Adenosine Triphosphate Activities in Red Blood Cells of People With Sickle Cell Disease

👨‍⚕️ Swee Lay Thein, M.D., National Heart, Lung, and Blood Institute (NHLBI)📍 1 site📅 Started Oct 2018View details ↗
Phase 1RecruitingNCT03653338

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

👨‍⚕️ Paul Szabolcs, MD, University of Pittsburgh📍 1 site📅 Started Aug 2018View details ↗

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