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Showing 8 of 8 recruiting trials for “Proximal myotonic myopathy

Phase 3Enrolling by InvitationNCT06549400

An Open-Label Extension Study to Evaluate the Long-Term Safety and Efficacy of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2 Who Have Completed MEX-DM-302 Study.

🏥 Lupin Ltd.📍 6 sites📅 Started Sep 2025View details ↗
Phase 1, PHASE2RecruitingNCT06844214

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 50 Years of Age With Non-congenital Myotonic Dystrophy Type 1

🏥 Sanofi📍 8 sites📅 Started Jul 2025View details ↗
NARecruitingNCT06716931

Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)

🏥 Massachusetts General Hospital📍 1 site📅 Started Mar 2025View details ↗
Phase 3RecruitingNCT06523400

The Efficacy and Safety of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2

🏥 Lupin Ltd.📍 7 sites📅 Started Feb 2025View details ↗
RecruitingNCT05854433

Brain Structure and Clinical Endpoints in Myotonic Dystrophy Type 2

👨‍⚕️ Araya Puwanant, MD, MS, Wake Forest University Health Sciences📍 1 site📅 Started Apr 2023View details ↗
RecruitingNCT04003363

The United Kingdom National Registry for Myotonic Dystrophy

👨‍⚕️ Chiara Marini-Bettolo, MD, PhD, John Walton Muscular Dystrophy Research Centre📍 1 site📅 Started May 2013View details ↗
RecruitingNCT02398786

Myotonic Dystrophy Family Registry

👨‍⚕️ Tanya Stevenson, EdD, MPH, Myotonic Dystrophy Foundation📍 1 site📅 Started Feb 2013View details ↗
RecruitingNCT00082108

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

👨‍⚕️ Johann Hamel, MD, University of Rochester Medical Center, Department of Neurology📍 1 site📅 Started Sep 2000View details ↗

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