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Showing 1 of 1 recruiting trials for “Posterior column ataxia-retinitis pigmentosa syndrome

EARLY_Phase 1Enrolling by InvitationNCT06565572

Antisense Oligonucleotide Treatment for PCARP Disease Due to Mutation in FLVCR1

🏥 University of Colorado, Denver📍 1 site📅 Started Aug 2023View details ↗

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