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Showing 14 of 14 recruiting trials for “Phenylketonuria

Phase 3RecruitingNCT06971731

A Study to Evaluate the Safety and Efficacy of JNT-517 in Participants With Phenylketonuria (PKU)

👨‍⚕️ Otsuka Call Center📍 20 sites📅 Started Oct 2025View details ↗
NARecruitingNCT06941532

GMP Powdered Substitutes in PKU and TYR

👨‍⚕️ Gary Hubbard, Dr, Nutricia UK Ltd📍 1 site📅 Started May 2025View details ↗
NAEnrolling by InvitationNCT06940193

A Self-test Home-use Blood Phenylalanine Monitoring System Under the Brand Name Egoo Phe System Has Been Developed for Measurement of Phenylalanine (Phe) in Individuals Diagnosed With Phenylketonuria (PKU): The Study Purpose is to Evaluate Accuracy and Usability

👨‍⚕️ Anita MacDonald, Birmingham Women's and Children's NHS Foundation Trust📍 1 site📅 Started Apr 2025View details ↗
NARecruitingNCT06969209

Brain Aging in Phenylketonuria

👨‍⚕️ Regula Everts, Prof. Dr. phil., Department of Diabetes, Endocrinology, Nutritional Medicine and Metabolism, Inselspital, Bern University Hospital and University of Bern, Switzerland📍 1 site📅 Started Jan 2025View details ↗
Phase 1RecruitingNCT06332807

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

👨‍⚕️ Study Contact📍 5 sites📅 Started Jan 2025View details ↗
NARecruitingNCT06560736

Development of Novel Psychological Assessment Tools and Anxiety Intervention for Phenylketonuria

👨‍⚕️ Shawn Christ📍 1 site📅 Started Oct 2024View details ↗
NARecruitingNCT06718842

Walking Program in Fatty Liver Children With Phenylketonuria

👨‍⚕️ Ali Ismail, lecturer, Cairo University📍 1 site📅 Started Sep 2024View details ↗
Phase 1RecruitingNCT06687733

Safety and Efficacy Study of NGGT002 in cPKU Adult Subjects

👨‍⚕️ Jianping Weng, PhD, First Affiliated Hospital of Bengbu Medical College📍 2 sites📅 Started Jul 2024View details ↗
Phase 3RecruitingNCT06302348

A Study of Sepiapterin in Participants With Phenylketonuria (PKU)

👨‍⚕️ Patient Advocacy📍 1 site📅 Started Mar 2024View details ↗
NARecruitingNCT06305234

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

👨‍⚕️ Medical Director, MD, BioMarin Pharmaceutical📍 6 sites📅 Started Jan 2024View details ↗
EARLY_Phase 1RecruitingNCT06061614

Safety and Efficacy Study of NGGT002 in PKU Adult Subjects

👨‍⚕️ Huan Zhou, Doctor📍 1 site📅 Started Mar 2023View details ↗
NARecruitingNCT05813678

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

👨‍⚕️ Medical Director, MD, BioMarin Pharmaceutical📍 16 sites📅 Started Jun 2022View details ↗
NARecruitingNCT05128149

Metabolic Control and Patient Well-being in Phenylketonuria: do Guidelines Make a Difference?

👨‍⚕️ Martina Huemer, Prof📍 1 site📅 Started Nov 2021View details ↗
NAEnrolling by InvitationNCT04348708

Long-Term Follow Up Study of Subjects Previously Administered HMI 102

🏥 Homology Medicines, Inc📍 2 sites📅 Started Aug 2020View details ↗

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