🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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Showing 2 of 2 recruiting trials for “Pelizaeus-Merzbacher disease”

Phase 1RecruitingNCT06150716 ↗

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

🏥 Ionis Pharmaceuticals, Inc.📍 7 sites📅 Started Apr 2024View details ↗
RecruitingNCT05659901 ↗

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

🏥 Ionis Pharmaceuticals, Inc.📍 8 sites📅 Started Oct 2022View details ↗

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