🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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6+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 6 of 6 recruiting trials for “Ornithine transcarbamylase deficiency”

RecruitingNCT06805695 ↗

Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)

👨‍⚕️ George Diaz, M.D., Ph.D, iECURE, Inc.📍 1 site📅 Started Dec 2024View details ↗
Phase 2RecruitingNCT06488313 ↗

A Study to Evaluate the Pharmacodynamics and Safety of ARCT-810 in Participants With OTCD

🏥 Arcturus Therapeutics, Inc.📍 1 site📅 Started Nov 2024View details ↗
Phase 1, PHASE2RecruitingNCT06255782 ↗

An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency

👨‍⚕️ George Diaz, M.D., Ph.D, iECURE, Inc.📍 10 sites📅 Started Apr 2024View details ↗
Phase 1, PHASE2RecruitingNCT05092685 ↗

Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEn

👨‍⚕️ Federicco Mingozzi, Genethon📍 1 site📅 Started Nov 2023View details ↗
RecruitingNCT04908319 ↗

Hepatic Histopathology in Urea Cycle Disorders

👨‍⚕️ Lindsay Burrage, MD, PhD, Baylor College of Medicine📍 2 sites📅 Started Feb 2022View details ↗
RecruitingNCT04612764 ↗

Liver Disease in Urea Cycle Disorders

👨‍⚕️ Lindsay Burrage, MD, PhD, Baylor College of Medicine📍 5 sites📅 Started Nov 2021View details ↗

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