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Showing 2 of 2 recruiting trials for “Ocular cystinosis

Phase 1RecruitingNCT06910813

DFT383 in Pediatric Participants With Nephropathic Cystinosis

👨‍⚕️ Novartis Pharmaceuticals📍 4 sites📅 Started Jun 2025View details ↗
NARecruitingNCT03919981

CYSTEA-BONE Clinical Study

👨‍⚕️ Justine BACCHETTA, MD PhD📍 13 sites📅 Started Apr 2019View details ↗

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