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17+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 17 of 17 recruiting trials for “OBSOLETE: Inherited retinal disorder

Phase 1, PHASE2RecruitingNCT07408232

A Phase 1/2 Study in Healthy Volunteers and Participants With Autosomal Dominant Retinitis Pigmentosa (RHO-adRP)

🏥 Octant, Inc.📍 1 site📅 Started Feb 2026View details ↗
EARLY_Phase 1RecruitingNCT07063030

A Study of LX107 Gene Therapy in AIPL1-IRD Patients

🏥 Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine📍 1 site📅 Started Jul 2025View details ↗
Phase 1, PHASE2RecruitingNCT06852963

A Repeat-Dose, Open-Label, Two Arm Safety and Efficacy Study of Two Doses of VP-001 Administered Intravitreally in Participants With Confirmed PRPF31 Mutation-Associated Retinal Dystrophy, Including Participants Previously Treated With VP001

🏥 PYC Therapeutics📍 6 sites📅 Started Jun 2025View details ↗
Phase 1RecruitingNCT06319872

The Effects of Disulfiram (Antabuse®) on Visual Acuity in Patients With Retinal Degeneration

🏥 University of Rochester📍 1 site📅 Started May 2025View details ↗
Phase 1RecruitingNCT06936787

An Open-label, Dose-ascending Study of IGT001 for Retinitis Pigmentosa

🏥 Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine📍 1 site📅 Started Apr 2025View details ↗
Enrolling by InvitationNCT07056738

Prospective Exploratory Cohort Study on Ganglion Cell Degeneration in Retinitis Pigmentosa Patients

👨‍⚕️ Emilie Macé, Professor, Else Kroener Fresenius Center for Optogenetic Therapies, University Medical Center Goettingen📍 1 site📅 Started Mar 2025View details ↗
Phase 1RecruitingNCT06455826

MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby)

🏥 PYC Therapeutics📍 5 sites📅 Started Jun 2024View details ↗
EARLY_Phase 1RecruitingNCT06292650

Safety and Efficacy Study of Novel Gene Therapy ZM-02 for Retinitis Pigmentosa Patients

👨‍⚕️ Wenbin Wei, PhD, Beijing Tongren Hospital, CMU📍 1 site📅 Started Feb 2024View details ↗
RecruitingNCT06323772

Natural History Study in Patients with PDE6A-, PDE6B- and RHO-linked Retinitis Pigmentosa

👨‍⚕️ Katarina Stingl, Prof, Department for Opthalmology📍 1 site📅 Started Nov 2023View details ↗
Phase 3RecruitingNCT05926583

A Study of AAV5-hRKp.RPGR for the Treatment of Japanese Participants With X-linked Retinitis Pigmentosa

👨‍⚕️ Janssen Pharmaceutical K.K., Japan Clinical Trial, Janssen Pharmaceutical K.K.📍 1 site📅 Started Sep 2023View details ↗
EARLY_Phase 1RecruitingNCT05805007

Safety and Tolerability Study of Gene Editing Drug ZVS203e in Participants With Retinitis Pigmentosa

👨‍⚕️ Liping Yang, MD, Peking University Third Hospital📍 1 site📅 Started Sep 2023View details ↗
Phase 1RecruitingNCT06291935

Safety and Tolerability of Intravitreal Administration of VG901 in Patients With Retinitis Pigmentosa Due to Mutations in the CNGA1 Gene

👨‍⚕️ Katarina Stingl, Center for Ophthalmology, University of Tuebingen📍 1 site📅 Started Sep 2023View details ↗
Enrolling by InvitationNCT05921162

A Long-Term Follow-Up Study in Subjects Who Received vMCO-I Administered Via Intravitreal Injection

👨‍⚕️ Samarendra Mohanty, Nanoscope Therapeutics Inc.📍 1 site📅 Started Jul 2023View details ↗
Phase 1, PHASE2RecruitingNCT05748873

Promising ROd-cone DYstrophy Gene therapY

🏥 SparingVision📍 6 sites📅 Started Apr 2023View details ↗
Phase 1RecruitingNCT05147701

Safety of Cultured Allogeneic Adult Umbilical Cord Derived Mesenchymal Stem Cells for NAION

👨‍⚕️ Chadwick Prodromos, MD, The Foundation for Orthopaedics and Regenerative Medicine📍 2 sites📅 Started Feb 2022View details ↗
RecruitingNCT04658251

Study of New Mutations in Cone Disorders

👨‍⚕️ Claire-Marie DHAENENS, MD, University Hospital, Lille📍 1 site📅 Started Mar 2021View details ↗
RecruitingNCT02471287

Genetics of Inherited Eye Disease

👨‍⚕️ Laryssa A Huryn, M.D., National Eye Institute (NEI)📍 1 site📅 Started Jun 2015View details ↗

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