🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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2+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 2 of 2 recruiting trials for “Leber congenital amaurosis”

Phase 3RecruitingNCT06891443 ↗

Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

🏥 Laboratoires Thea📍 14 sites📅 Started Jun 2025View details ↗
Phase 1, PHASE2RecruitingNCT05906953 ↗

Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)

👨‍⚕️ Study Director, HuidaGene Therapeutics Co., Ltd.📍 3 sites📅 Started Oct 2023View details ↗

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