🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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9+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 9 of 9 recruiting trials for “Homozygous familial hypercholesterolemia”

Phase 2RecruitingNCT07489209 ↗

A Dose-exploration Study of EDP167 in HoFH

👨‍⚕️ Kefei Dou, MD, Chinese Academy of Medical Sciences, Fuwai Hospital📍 1 site📅 Started Feb 2026View details ↗
Phase 3RecruitingNCT07037771 ↗

A Phase 3 Study of Zodasiran in Adolescent and Adult Subjects With Homozygous Familial Hypercholesterolemia (YOSEMITE)

🏥 Arrowhead Pharmaceuticals📍 22 sites📅 Started Jun 2025View details ↗
NARecruitingNCT06743659 ↗

Computerized Decision Support for Identification and Management of Familial Hypercholesterolemia

🏥 Brigham and Women's Hospital📍 1 site📅 Started Apr 2025View details ↗
EARLY_Phase 1RecruitingNCT06458010 ↗

Clinical Exploration Trial of YOLT-101 in the Treatment of Familial Hypercholesterolemia (FH)

🏥 RenJi Hospital📍 1 site📅 Started May 2024View details ↗
EARLY_Phase 1RecruitingNCT06125847 ↗

NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia

👨‍⚕️ Zuyi Yuan, M.D., First Affiliated Hospital of Xian Jiaotong University📍 1 site📅 Started Oct 2023View details ↗
NARecruitingNCT06571630 ↗

PMMHRI - Familial Hypercholesterolemia Registry

👨‍⚕️ Maciej Banach, MD,PhD,FNLA,FAHA,FESC,FASA📍 1 site📅 Started Jan 2018View details ↗
RecruitingNCT04815005 ↗

HoFH, the International Clinical Collaborators Registry

👨‍⚕️ Marina Cuchel, MD, PhD, University of Pennsylvania📍 4 sites📅 Started Jan 2017View details ↗
RecruitingNCT02135705 ↗

LOWER: Lomitapide Observational Worldwide Evaluation Registry

👨‍⚕️ Janet Boylan, Amryt Pharmaceuticals📍 75 sites📅 Started Mar 2014View details ↗
RecruitingNCT01109368 ↗

The Rogosin Institute Homozygous Familial Hypercholesterolemia Repository

👨‍⚕️ Lisa C. Hudgins, M.D., The Rogosin Institute📍 1 site📅 Started Jun 2010View details ↗

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