🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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Showing 2 of 2 recruiting trials for “Hereditary Erythropoietic Porphyria”

Phase 1, PHASE2RecruitingNCT07024316 ↗

A Study to Investigate the Improvement of Photosensitivity in Terms of Skin Lesions Associated With CEP Following Administration of Oral ATL-001 (Ciclopirox Oral Solution) in Participants Aged >18 Years of Age With CEP

🏥 Atlas Molecular Pharma📍 1 site📅 Started Jan 2026View details ↗
Phase 2, PHASE3Enrolling by InvitationNCT05883748 ↗

HELIOS: Open-Label, Long-Term Extension Study to Investigate the Safety, Tolerability, and Efficacy of DISC-1459 (Bitopertin) in Participants With EPP or XLP

👨‍⚕️ Will Savage, MD PhD, Disc Medicine📍 13 sites📅 Started Aug 2023View details ↗

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