🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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3+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 3 of 3 recruiting trials for “Familial platelet disorder with associated myeloid malignancy”

Phase 2RecruitingNCT06261060 ↗

Low-Dose Sirolimus to Increase Hematopoietic Function in Patients With RUNX1 Familial Platelet Disorder

👨‍⚕️ Courtney DiNardo, MD, M.D. Anderson Cancer Center📍 1 site📅 Started Jun 2024View details ↗
Phase 1RecruitingNCT06414889 ↗

Protocol Title: Safety and Feasibility of Autologous CD34+ Hematopoietic Stem Cells Mobilization and Apheresis in Participants With RUNX1 Familial Platelet Disorder

👨‍⚕️ Chitra Hosing, M.D. Anderson Cancer Center📍 1 site📅 Started May 2024View details ↗
RecruitingNCT03854318 ↗

Longitudinal Studies of Patient With FPDMM

👨‍⚕️ Paul Liu, M.D., National Human Genome Research Institute (NHGRI)📍 1 site📅 Started Mar 2019View details ↗

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