🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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3+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Showing 3 of 3 recruiting trials for “Danon disease

RecruitingNCT06214507

Danon Disease Natural History Study

🏥 Rocket Pharmaceuticals Inc.📍 13 sites📅 Started Dec 2023View details ↗
Phase 2RecruitingNCT06092034

A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease

👨‍⚕️ Joseph Rossano, MD, Children's Hospital of Philadelphia📍 6 sites📅 Started Sep 2023View details ↗
NARecruitingNCT07336394

Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance Techniques

👨‍⚕️ Minjie Lu MD, PhD📍 1 site📅 Started Jan 2010View details ↗

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