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Showing 13 of 13 recruiting trials for “Chronic granulomatous disease

Phase 2RecruitingNCT07284641

Hematopoietic Stem Cell Transplantation (HSCT) for Common Variable Immunodeficiency (CVID) and Other Autoimmune Manifestations of Primary Immune Regulatory Disorders (PIRD)

👨‍⚕️ Paul Szabolcs, MD, UPMC Children's Hospital of Pittsburgh📍 1 site📅 Started Mar 2026View details ↗
Phase 1Enrolling by InvitationNCT07113743

Part B- G1X-CGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease

👨‍⚕️ Elizabeth M Kang, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Sep 2025View details ↗
Phase 1, PHASE2RecruitingNCT06876363

Study of EN-374 Gene Therapy in Participants With X-Linked Chronic Granulomatous Disease

🏥 Ensoma📍 9 sites📅 Started Aug 2025View details ↗
RecruitingNCT06605378

Prevalence of Antibodies and Cytokines in Participants With Chronic Granulomatous Disease

🏥 Ensoma📍 52 sites📅 Started Nov 2024View details ↗
Phase 1, PHASE2Enrolling by InvitationNCT06253507

pCCLCHIM-p47 (Lentiviral Vector Transduced CD34 Plus Cells) in Patients With p47 Autosomal Recessive Chronic Granulomatous Disease (AR-CGD)

👨‍⚕️ Elizabeth M Kang, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Jun 2024View details ↗
Phase 1RecruitingNCT06325709

Base Editing for Mutation Repair in Hematopoietic Stem & Progenitor Cells for X-Linked Chronic Granulomatous Disease

👨‍⚕️ Suk S De Ravin, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Apr 2024View details ↗
Phase 1, PHASE2Enrolling by InvitationNCT05104723

Safety and Efficacy of Tofacitinib for Chronic Granulomatous Disease With Inflammatory Complications

👨‍⚕️ Christa S Zerbe, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Aug 2022View details ↗
Phase 1, PHASE2RecruitingNCT05333471

Fecal Microbiota Transplantation for Chronic Granulomatous Disease-Associated Colitis

👨‍⚕️ Suchitra K Hourigan, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Aug 2022View details ↗
Phase 1RecruitingNCT05189925

NADPH Oxidase Correction in mRNA-transfected Granulocyte-enriched Cells in Chronic Granulomatous Disease (CGD)

👨‍⚕️ Suk S De Ravin, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Jul 2022View details ↗
Phase 1, PHASE2RecruitingNCT05463133

Allogeneic Hematopoietic Stem Cell Transplantation for Chronic Granulomatous Disease (CGD) With an Alemtuzumab, Busulfan and TBI-based Conditioning Regimen Combined With Cytokine (IL-6, +/- IFN-gamma) Antagonists

👨‍⚕️ Elizabeth M Kang, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Jul 2022View details ↗
Phase 2RecruitingNCT03055247

Combination of Ibuprofen, G-CSF and Plerixafor as Stem Cells Mobilization Regimen in Patients Affected by X-CGD

👨‍⚕️ Fabio Ciceri, MD, PhD, Ospedale San Raffaele📍 2 sites📅 Started Nov 2015View details ↗
RecruitingNCT00128973

Evaluation of Patients With Immune Function Abnormalities

👨‍⚕️ Harry L Malech, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Sep 2005View details ↗
NARecruitingNCT00001405

Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granulocytes

👨‍⚕️ Harry L Malech, M.D., National Institute of Allergy and Infectious Diseases (NIAID)📍 1 site📅 Started Feb 1994View details ↗

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