🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

Find Clinical Trials for Your Rare Disease

1+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

Clinical trial records are synced from ClinicalTrials.gov.
Report missing data
Clear

Showing 1 of 1 recruiting trials for “Autosomal dominant Charcot-Marie-Tooth disease type 2D

Phase 1, PHASE2Enrolling by InvitationNCT07226297

Personalized Antisense Oligonucleotide for A Single Participant With GARS1 Gene Mutation Associated With Charcot-Marie-Tooth Disease Type 2D (CMT2D)

🏥 n-Lorem Foundation📍 1 site📅 Started Oct 2025View details ↗

Get alerts when new trials open

Create a free account to follow conditions and receive trial notifications.

Create free account →