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Showing 2 of 2 recruiting trials for “Aromatic L-amino acid decarboxylase deficiency

EARLY_Phase 1RecruitingNCT05765981

An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

👨‍⚕️ Jiwen Wang, Doctor, Shanghai Children's Medical Center, affiliated to Shanghai Jiao Tong University School of Medicine📍 1 site📅 Started Jan 2023View details ↗
Phase 1RecruitingNCT02852213

A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients

👨‍⚕️ Krystof Bankiewicz, MD, PhD, OSU Professor of Neurological Surgery📍 3 sites📅 Started Jul 2016View details ↗

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