🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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Showing 2 of 2 recruiting trials for “Acid sphingomyelinase deficiency

RecruitingNCT06192576

A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)

🏥 Sanofi📍 5 sites📅 Started Apr 2024View details ↗
NAEnrolling by InvitationNCT05368038

ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program

👨‍⚕️ Melissa Wasserstein, MD, Albert Einstein College of Medicine📍 9 sites📅 Started May 2021View details ↗

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