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Showing 11 of 11 recruiting trials for “Achondroplasia

RecruitingNCT07388966

Prospective Longitudinal Monocentric Study to Measure Limb Movement in Patients With FGFR3-related Skeletal Dysplasia

👨‍⚕️ Genevieve Baujat, Hopital Necker📍 1 site📅 Started Feb 2026View details ↗
Phase 2RecruitingNCT07169279

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

🏥 QED Therapeutics, a BridgeBio company📍 13 sites📅 Started Nov 2025View details ↗
RecruitingNCT07301463

A Study in Children With Achondroplasia

👨‍⚕️ Yuan Lu, 12B, Building 1, No 515, Huanke Road, Pudong New Area, Shanghai 201210, China📍 8 sites📅 Started Jun 2025View details ↗
Phase 2RecruitingNCT06842355

A Study of TYRA-300 in Children With Achondroplasia: BEACH301

👨‍⚕️ Doug Warner, MD, Tyra Biosciences📍 13 sites📅 Started Mar 2025View details ↗
Phase 2RecruitingNCT06732895

A Clinical Trial to Evaluate Efficacy and Safety of Navepegritide in Adolescents (12 - 18 Years of Age) With Achondroplasia.

👨‍⚕️ Medical Director, MD, Ascendis Pharma A/S📍 5 sites📅 Started Dec 2024View details ↗
Phase 3RecruitingNCT06926491

Evaluate the Efficacy and Safety of KK8398 in Patients With Achondroplasia(AOBA Study)

👨‍⚕️ Yu Sato, Kyowa Kirin Co., Ltd.📍 9 sites📅 Started Dec 2024View details ↗
Phase 2RecruitingNCT06079398

A Clinical Trial to Evaluate Efficacy and Safety of TransCon CNP Compared With Placebo in Infants (0 to <2 Years of Age) With Achondroplasia

👨‍⚕️ Medical Director, MD, Ascendis Pharma A/S📍 17 sites📅 Started Jan 2024View details ↗
Phase 2, PHASE3Enrolling by InvitationNCT05929807

A Clinical Trial to Investigate Long-term Safety, Tolerability, and Efficacy of Weekly Subcutaneous Doses With TransCon CNP in Children and Adolescents With Achondroplasia

👨‍⚕️ Claus Strange, Ascendis Pharma A/S📍 17 sites📅 Started Jun 2023View details ↗
RecruitingNCT06168201

VIrtual STudy in Achondroplasia for the US (VISTA)

👨‍⚕️ Medical Director, MD, BioMarin Pharmaceutical📍 7 sites📅 Started Feb 2023View details ↗
Phase 2Enrolling by InvitationNCT05145010

Extension Study of Infigratinib in Children With Achondroplasia (ACH)

👨‍⚕️ QED Therapeutics SVP, Clinical Development, QED Therapeutics📍 31 sites📅 Started Dec 2021View details ↗
RecruitingNCT05328050

Registry for Patients With Achondroplasia / Hypochondroplasia (OMPR-Ach/Hy)

🏥 Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico📍 1 site📅 Started Sep 2021View details ↗

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