Showing 2 of 2 recruiting trials for “3-hydroxy-3-methylglutaric-aciduria”
An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)
👨⚕️ Gerard Vockley, MD, PhD, UPMC Children's Hospital of Pittsburgh📍 1 site📅 Started Jul 2025View details ↗
Enrolling by InvitationNCT01803906 ↗
Tissue Sample Study for Mitochondrial Disorders
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