🧪 UPDATED DAILY FROM CLINICALTRIALS.GOVSynced Apr 1

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1+ recruiting trials across all rare diseases. Filter by phase, location, and condition.

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Clinical trial records are synced from ClinicalTrials.gov.

Showing 1 of 1 recruiting trials for “2-hydroxyglutaric aciduria”

Phase 1Enrolling by InvitationNCT07125066 ↗

An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)

👨‍⚕️ Gerard Vockley, MD, PhD, UPMC Children's Hospital of Pittsburgh📍 1 site📅 Started Jul 2025View details ↗

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