24VA021; VATCH Trametinib for Ras/MAPK Pathway VAs
Studying Cerebellar ataxia with neuropathy and bilateral vestibular areflexia syndrome
Last synced from ClinicalTrials.gov
Key facts
- Sponsor
- Children's Hospital of Philadelphia
- Intervention
- Trametinib(drug)
- Enrollment
- 45 target
- Eligibility
- 30 years · All sexes
- Timeline
- 2025 – 2030
Study locations (1)
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Collaborators
Novartis · CaNVAS (Consortium of Investigators of Vascular Anomalies) · Texas Children's · Arkansas Children's Hospital Research Institute · Nationwide Children's Hospital · Nemours Children's Health · Boston Children's Hospital · NYU Langone Health · Children's Healthcare of Atlanta · Oregon Health and Science University · Children's Hospital Colorado · Riley Children's Health · Children's Hospital of Los Angeles (CHLA) · Seattle Children's Hospital · Children's Hospital of Orange County (CHOC) · Children's Wisconsin - Milwaukee · University of North Carolina · Children's Hospital Medical Center, Cincinnati · University of California, San Francisco · Columbia University · Children's Hospital of Pittsburg · Dell Children's Medical Center of Central Texas · Vanderbilt University Medical Center · Helen DeVos Children's Hospital · Washington University School of Medicine · Lucile Packard Children's Hospital Stanford
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT07549646 on ClinicalTrials.govOther trials for Cerebellar ataxia with neuropathy and bilateral vestibular areflexia syndrome
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See all trials for Cerebellar ataxia with neuropathy and bilateral vestibular areflexia syndrome →