Active, not recruitingPHASE1, PHASE2NCT07221760
Personalized Antisense Oligonucleotide for A Single Participant (nL62541) With ATN1 Gene Mutation
Studying Dentatorubral pallidoluysian atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- n-Lorem Foundation
- Intervention
- nL-ATN1-001(drug)
- Enrollment
- 1 enrolled
- Eligibility
- 22 years · MALE
- Timeline
- 2025 – 2027
Study locations (1)
- Dell Children's, Austin, Texas, United States
Collaborators
Dell Children's Medical Center of Central Texas
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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