Enrolling by invitationPhase 1NCT07125066
An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)
Studying 2-hydroxyglutaric aciduria
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Jerry Vockley, MD, PhD
- Principal Investigator
- Gerard Vockley, MD, PhD, MD, PhDUPMC Children's Hospital of Pittsburgh
- Intervention
- Sodium phenylbutyrate(drug)
- Enrollment
- 1 enrolled
- Eligibility
- MALE
- Timeline
- 2025 – 2027
Study locations (1)
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh, Pennsylvania, United States
Collaborators
Zevra Therapeutics
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT07125066 on ClinicalTrials.gov