RecruitingPhase 1NCT06910813
DFT383 in Pediatric Participants With Nephropathic Cystinosis
Studying Ocular cystinosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Novartis Pharmaceuticals
- Principal Investigator
- Novartis Pharmaceuticals
- Intervention
- DFT383(genetic)
- Enrollment
- 30 enrolled
- Eligibility
- 2-5 years · All sexes
- Timeline
- 2025 – 2031
Study locations (4)
- University of California at San Diego - Rady Children's Hospital, San Diego, California, United States
- Stanford University - Stanford Children's Health, Stanford, California, United States
- Emory University School of Medicine - Children's Healthcare of Atlanta (recuiting Cohort 0), Atlanta, Georgia, United States
- Baylor College of Medicine - Texas Children's Hospital (recuiting Cohort 0), Houston, Texas, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06910813 on ClinicalTrials.govOther trials for Ocular cystinosis
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