RecruitingPhase 1NCT06858397
A proof-of Concept Study to Assess Safety and Tolerability of HM15421/GC1134A in Patients With Fabry Disease
Studying Fabry disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- GC Biopharma Corp
- Principal Investigator
- GC Biopharma
- Intervention
- HM15421/GC1134A(drug)
- Enrollment
- 18 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2025 – 2028
Study locations (10)
- David Geffen School of Medicine UCLA, UCLA Health, Los Angeles, California, United States
- University of Kansas School of Medicine, Kansas City, Kansas, United States
- University of Minnesota, Minneapolis, Minnesota, United States
- Children's Hospital Medical Center, Cincinnati, Ohio, United States
- University of Pittsburgh Medical Center Children's Hoispital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center, Fairfax, Virginia, United States
- Centro Medico IPAM, Rosario, Santa Fe Province, Argentina
- Hospital Italiano de Buenos Aires, Buenos Aires, Argentina
- Pusan National University Children's Hospital in Yangsan, Yangsan, Gyeongsangnam-do, South Korea
- Yonsei University, College of Medicine, Seoul, South Korea
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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