Active, not recruitingNCT06614569
Long-Term Follow-Up of Subjects Treated With AXO-AAV-GM2 for Tay-Sachs or Sandhoff Disease
Studying GM2 gangliosidosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Terence Flotte
- Principal Investigator
- Terence Flotte, MDUMass Chan Medical School
- Intervention
- AXO-AAV-GM2(drug)
- Enrollment
- 7 enrolled
- Eligibility
- All sexes
- Timeline
- 2024 – 2028
Study locations (1)
- UMass Chan Medical School, Worcester, Massachusetts, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06614569 on ClinicalTrials.govOther trials for GM2 gangliosidosis
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