RecruitingNCT06581146
A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
Studying X-linked centronuclear myopathy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Astellas Gene Therapies
- Principal Investigator
- Medical DirectorAstellas Gene Therapies
- Intervention
- No Intervention(other)
- Enrollment
- 50 enrolled
- Eligibility
- 17 years · MALE
- Timeline
- 2025 – 2027
Study locations (5)
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06581146 on ClinicalTrials.govOther trials for X-linked centronuclear myopathy
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