Active, not recruitingPHASE1, PHASE2NCT06314490
Personalized Antisense Oligonucleotide Therapy for Rare Pediatric Genetic Disease: SCN2A
Studying Rare genetic disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- University of California, San Diego
- Principal Investigator
- Olivia Kim-McManus, M.D.UCSD Rady Children's Hospital
- Intervention
- nL-SCN2A-002(drug)
- Enrollment
- 1 enrolled
- Eligibility
- All sexes
- Timeline
- 2024 – 2026
Study locations (1)
- Rady Children's Hospital, San Diego, California, United States
Collaborators
California Institute for Regenerative Medicine (CIRM) · n-Lorem Foundation
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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