RecruitingEarly Phase 1NCT06207552
Evaluation of the Safety, Tolerability and Efficacy of a Gene Therapy Drug for the Treatment of Pediatric Fabry Disease
Studying Fabry disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Children's Hospital of Fudan University
- Principal Investigator
- Hong Xu, MD,PhDChildren's Hospital of Fudan University
- Intervention
- BBM-F101 injection(genetic)
- Enrollment
- 6 enrolled
- Eligibility
- 7-18 years · All sexes
- Timeline
- 2024 – 2029
Study locations (1)
- Children's Hospital of Fudan University, Shanghai, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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