RecruitingPhase 1NCT06150716
Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
Studying Pelizaeus-Merzbacher disease
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Ionis Pharmaceuticals, Inc.
- Intervention
- ION356(drug)
- Enrollment
- 24 enrolled
- Eligibility
- 2-17 years · MALE
- Timeline
- 2024 – 2028
Study locations (7)
- Ionis Investigative Site, Atlanta, Georgia, United States
- Ionis Investigative Site, Philadelphia, Pennsylvania, United States
- Ionis Investigative Site, Salt Lake City, Utah, United States
- Ionis Investigative Site, Le Kremlin-Bicêtre, France
- Ionis Investigative Site, Göttingen, Germany
- Ionis Investigative Site, Tokyo, Japan
- Ionis Investigative Site, Amsterdam, Netherlands
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06150716 on ClinicalTrials.govOther trials for Pelizaeus-Merzbacher disease
Additional recruiting or active studies for the same condition.