Active, not recruitingPhase 1NCT05973630
ATA-200 Gene Therapy Trial in Patients With LGMDR5
Studying Gamma-sarcoglycan-related limb-girdle muscular dystrophy R5
Last synced from ClinicalTrials.gov
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Report missing dataKey facts
- Sponsor
- Atamyo Therapeutics
- Intervention
- ATA-200(biological)
- Enrollment
- 4 enrolled
- Eligibility
- 6-13 years · All sexes
- Timeline
- 2025 – 2031
Study locations (1)
- Child Health Research Institute, Gainsville, Florida, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT05973630 on ClinicalTrials.gov