RecruitingPhase 3NCT05898620
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
Studying Rett syndrome
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Neurogene Inc.
- Principal Investigator
- Julie Jordan, MD, MDNeurogene Inc.
- Intervention
- NGN-401(genetic)
- Enrollment
- 33 enrolled
- Eligibility
- 3 years · FEMALE
- Timeline
- 2023 – 2029
Study locations (16)
- University of Alabama at Birmingham, Birmingham, Alabama, United States
- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- Children's Hospital Colorado, Aurora, Colorado, United States
- Nicklaus Children's Hospital Research Institute, Miami, Florida, United States
- Rush University Medical Center, Chicago, Illinois, United States
- Kennedy Krieger Institute, Baltimore, Maryland, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Montefiore Medical Center, New York, New York, United States
- UNC at Chapel Hill, Chapel Hill, North Carolina, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Vanderbilt University Medical Center, Nashville, Tennessee, United States
- Texas Children's Hospital, Houston, Texas, United States
- The Children's Hospital at Westmead, Sydney, New South Wales, Australia
- Royal Hospital for Children and Young People, Edinburgh, United Kingdom
- +1 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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