UnknownPHASE1, PHASE2NCT05588401

Evaluating Safety and Efficacy of Autologous Gene-edited Muscle Stem Cells (GenPHSats-bASKet)

Studying Limb-girdle muscular dystrophy

Last synced from ClinicalTrials.gov April 1, 2026

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Key facts

Sponsor: Simone Spuler, MD
Principal Investigator: Simone Spuler, Prof Dr med
Charite Universitätsmedizin Berlin, Germany
Intervention: GenPHSat injection (Safety)(biological)
Enrollment: 6 target
Eligibility: 14 years · All sexes
Timeline: 2024 – 2025

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT05588401 on ClinicalTrials.gov

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