RecruitingPhase 1NCT05302271
Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia
Studying Friedreich ataxia
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Weill Medical College of Cornell University
- Principal Investigator
- Ronald G Crystal, MD, PharmDWeill Medical College of Cornell University
- Intervention
- AAVrh.10hFXN, serotype rh.10 adeno-associated virus (AAV) gene transfer vector expressing the cDNA coding for human FXN(biological)
- Enrollment
- 25 enrolled
- Eligibility
- 12-50 years · All sexes
- Timeline
- 2022 – 2029
Study locations (1)
- Weill Cornell Medicine, New York, New York, United States
Collaborators
National Heart, Lung, and Blood Institute (NHLBI)
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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