Study to Evaluate the Efficacy Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene With Early to Moderate Vision Loss (Celeste)

Key facts

Sponsor

Laboratoires Thea

Principal Investigator

Sepul Bio Chief Medical Officer

Sepul Bio

Intervention

QR-421a(drug)

Enrollment

5 enrolled

Eligibility

12 years · All sexes

Timeline

2021 – 2022

Study locations (3)

• Retina Foundation of the Southwest, Dallas, Texas, United States
• University of Wisconsin - Madison, Madison, Wisconsin, United States
• Moorfields Eye Hospital, London, United Kingdom

Collaborators

Sepul Bio

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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