Active, not recruitingPHASE1, PHASE2NCT04884815
A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease
Studying Wilson disease
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Ultragenyx Pharmaceutical Inc
- Principal Investigator
- Medical DirectorUltragenyx Pharmaceutical Inc
- Intervention
- UX701(genetic)
- Enrollment
- 82 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2021 – 2034
Study locations (16)
- University of California Los Angeles, Los Angeles, California, United States
- Stanford University, Redwood City, California, United States
- University of California Davis, Sacramento, California, United States
- Northwestern University, Chicago, Illinois, United States
- Indiana University, Indianapolis, Indiana, United States
- Massachusetts General Hospital, Boston, Massachusetts, United States
- University of Michigan, Ann Arbor, Michigan, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Vanderbilt University Medical Center, Nashville, Tennessee, United States
- University of Utah, Salt Lake City, Utah, United States
- Seattle Children's Hospital, Seattle, Washington, United States
- Gordon and Leslie Diamond Health Care Centre, Vancouver, British Columbia, Canada
- Centro Hospitalar Universitário Lisboa Norte, Lisbon, Lisbon District, Portugal
- Centro Hospitalar Universitário de São João, Porto, Porto District, Portugal
- Hospital Universitario Vall d'Hebron - PPDS, Barcelona, Spain
- +1 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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