RecruitingPHASE1, PHASE2NCT04819841
Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease
Studying Genetic hemoglobinopathy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Kamau Therapeutics
- Principal Investigator
- Mathew Porteus, MD, PhDKamau Therapeutics
- Intervention
- nula-cel Drug Product(genetic)
- Enrollment
- 15 enrolled
- Eligibility
- 12-40 years · All sexes
- Timeline
- 2021 – 2028
Study locations (4)
- Children's Hospital Los Angeles, Los Angeles, California, United States
- Lucile Packard Children's Hospital, Palo Alto, California, United States
- Washington University, St Louis, Missouri, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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