RecruitingPhase 3NCT04706013
Oral Pyridoxal 5'-Phosphate for the Treatment of Patients With PNPO Deficiency
Studying Pyridoxamine-5-phosphate deficiency-developmental and epileptic encephalopathy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Medicure
- Intervention
- Pyridoxal Phosphate(drug)
- Enrollment
- 15 enrolled
- Eligibility
- All sexes
- Timeline
- 2024 – 2026
Study locations (7)
- Children's Hospital of Alabama, Birmingham, Alabama, United States
- Lucile Packard Children's Hospital, Palo Alto, California, United States
- Children's Hospital Colorado, Aurora, Colorado, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Duke Children's Hospital, Durham, North Carolina, United States
- Akron's Children's Hospital, Akron, Ohio, United States
- Queensland Children's Hospital, South Brisbane, Queensland, Australia
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04706013 on ClinicalTrials.gov