CompletedPhase 2NCT04535609
An Efficacy and Safety Study of 24 Week Treatment With Mavodelpar (REN001) in Primary Mitochondrial Myopathy Patients
Studying Mitochondrial myopathy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Reneo Pharma Ltd
- Principal Investigator
- Amel Karaa, MDMassachusetts General Hospital (MGH)
- Intervention
- Mavodelpar(drug)
- Enrollment
- 213 target
- Eligibility
- 18 years · All sexes
- Timeline
- 2021 – 2023
Study locations (30)
- University of California, San Diego, La Jolla, California, United States
- Myology Institute, University of Florida, Gainesville, Florida, United States
- Massachusetts General Hospital, Boston, Massachusetts, United States
- Columbia University Irving Medical Center, New York, New York, United States
- Akron Children's Hospital, Akron, Ohio, United States
- The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University of Texas SouthWestern Medical Center, Dallas, Texas, United States
- Centre for the Treatment of Pediatric Neurodegenerative Disease, University of Texas McGovern Medical School, Houston, Texas, United States
- Royal North Shore Hospital, St Leonards, New South Wales, Australia
- PARC Clinical Research, Adelaide, South Australia, Australia
- The Alfred Hospital, Melbourne, Victoria, Australia
- University Hospital Leuven, Leuven, Belgium
- M.A.G.I.C. Clinic (Metabolics and Genetics in Calgary), Calgary, Alberta, Canada
- Adult Metabolic Diseases Clinic, Vancouver General Hospital, Vancouver, British Columbia, Canada
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04535609 on ClinicalTrials.govOther trials for Mitochondrial myopathy
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