Active, not recruitingPHASE1, PHASE2NCT04519749
An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease
Studying Fabry disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- 4D Molecular Therapeutics
- Principal Investigator
- Alan H Cohen, MD4D Molecular Therapeutics
- Intervention
- 4D-310(biological)
- Enrollment
- 18 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2020 – 2030
Study locations (4)
- University of California at San Diego, La Jolla, California, United States
- Emory University, Atlanta, Georgia, United States
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh, Pennsylvania, United States
- Lysosomal & Rare Disorders Research & Treatment Center, Inc, Fairfax, Virginia, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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