Active, not recruitingPHASE1, PHASE2NCT04480567
AAV Gene Therapy Study for Subjects with PKU
Studying Disorder of phenylalanine metabolism
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- BioMarin Pharmaceutical
- Principal Investigator
- Medical Director, MD, M.DBioMarin Pharmaceutical
- Intervention
- BMN 307(drug)
- Enrollment
- 100 enrolled
- Eligibility
- 15 years · All sexes
- Timeline
- 2020 – 2027
Study locations (3)
- University of South Florida, Tampa, Florida, United States
- Morristown Medical Center, Morristown, New Jersey, United States
- University Hospital Birmingham NHS Foundation Trust, Birmingham, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04480567 on ClinicalTrials.govOther trials for Disorder of phenylalanine metabolism
Additional recruiting or active studies for the same condition.
- RECRUITINGNANCT07220265Impact of Phenylalanine Elevations on Brain and Cognition in Adult PKU CarriersUniversity of Missouri-Columbia
- RECRUITINGPHASE2NCT06637514A Phase 2 Study of JNT-517 in Adolescent Participants With PhenylketonuriaOtsuka Pharmaceutical Development & Commercialization, Inc.
- RECRUITINGPHASE3NCT06628128A Study to Evaluate the Long-Term Safety and Efficacy of JNT-517 in Participants With PhenylketonuriaOtsuka Pharmaceutical Development & Commercialization, Inc.
- RECRUITINGNANCT05579548A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and BreastfeedingBioMarin Pharmaceutical