A Study of EPX-100 (Clemizole Hydrochloride) in Participants With Dravet Syndrome

Key facts

Sponsor

Epygenix

Principal Investigator

Amit Ray, MD

Harmony Biosciences Management, Inc.

Intervention

Clemizole HCl(drug)

Enrollment

150 enrolled

Eligibility

2 years · All sexes

Timeline

2020 – 2029

Study locations (30)

• Children's Hospital of Los Angeles, Los Angeles, California, United States
• University of California Irvine, Orange, California, United States
• UCSF Medical Center, San Francisco, California, United States
• Yale University School of Medicine, New Haven, Connecticut, United States
• The Nemours Foundation, Wilmington, Delaware, United States
• Rare Disease Research FL, Kissimmee, Florida, United States
• Pediatric Neurology and Epilepsy Specialists, Winter Park, Florida, United States
• Clinical Integrative Research Center of Atlanta (CIRCA), Atlanta, Georgia, United States
• Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
• Norton Children's Research Institute, Louisville, Kentucky, United States
• University of Michigan- Mott Children's Hospital, Ann Arbor, Michigan, United States
• Children's Nebraska, Omaha, Nebraska, United States
• Northeast Regional Epilepsy Group, Hackensack, New Jersey, United States
• Neurology Center for Epilepsy and Seizures, Marlboro, New Jersey, United States
• Weill Cornell Medical Center, New York, New York, United States
• +15 more locations on ClinicalTrials.gov

Collaborators

Harmony Biosciences Management, Inc.

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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See all trials for Dravet syndrome →