Interviews and Video Capture in Patients With GM1 Gangliosidosis

Key facts

Sponsor

LYSOGENE

Principal Investigator

Mindy Leffler, MEd

Casimir Trials

Intervention

Natural history(other)

Enrollment

25 enrolled

Eligibility

All sexes

Timeline

2020 – 2023

Study locations (1)

• Casimir Trials, Plymouth, Massachusetts, United States

Collaborators

Casimir, LLC · Cure GM1 Foundation

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Gangliosidosis

Additional recruiting or active studies for the same condition.

• RECRUITINGPHASE3NCT07082543
  A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis
  Azafaros A.G.
• RECRUITINGPHASE1, PHASE2NCT03952637
  A Phase 1/2 Study of Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 Gangliosidosis
  National Human Genome Research Institute (NHGRI)
• RECRUITINGNCT00668187
  A Natural History Study of the Gangliosidoses
  University of Minnesota

See all trials for Gangliosidosis →