Active, not recruitingPhase 2NCT04231266
Multi-Center Study of ManNAc for GNE Myopathy
Studying GNE myopathy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Leadiant Biosciences, Inc.
- Principal Investigator
- Anthony A. Amato, MD, MDBrigham and Women's Hospital
- Intervention
- ManNAc(drug)
- Enrollment
- 54 enrolled
- Eligibility
- 18-70 years · All sexes
- Timeline
- 2022 – 2025
Study locations (10)
- UCLA, Los Angeles, California, United States
- University of Iowa, Iowa City, Iowa, United States
- University of Kansas, Medical Center, Kansas City, Kansas, United States
- NIH Clinical Center, Bethesda, Maryland, United States
- Brigham and Women's Hospital, Boston, Massachusetts, United States
- Washington University, St Louis, Missouri, United States
- Columbia University Medical Center, New York, New York, United States
- University of Rochester, Rochester, New York, United States
- Ohio State University, Wexner Medical Center, Columbus, Ohio, United States
- University of Utah, Salt Lake City, Utah, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04231266 on ClinicalTrials.gov