WithdrawnPhase 3NCT04031066

Interventional Study to Assess Efficacy and Safety of Velmanase Alfa in Patients With Alpha Mannosidosis

Studying Alpha-mannosidosis

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Key facts

Sponsor
Chiesi Farmaceutici S.p.A.
Principal Investigator
Paul Harmatz, MD
UCSF Benioff Children's Hospital Oakland
Intervention
Velmanase Alfa(drug)
Eligibility
All sexes
Timeline
20212021

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT04031066 on ClinicalTrials.gov

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